National Institutes of Health

Recombinant DNA Advisory Committee (RAC)

 

92nd Meeting of the NIH RAC

 

Bethesda Marriott Hotel

Bethesda, Maryland

 

September 17-18, 2003

 

Meeting AgendA


 

Wednesday, September 17, 2003

 

10:30 AM        Call to Order and Opening Remarks

Theodore Friedmann, M.D., Chair, NIH RAC

 

Tab 2304         For Your Information

- Notice of Meeting

- Conflict of Interest Guidance

 

10:40 AM        Minutes of the June 18-19, 2003 RAC Meeting

                        Tab 2305

 

RAC Reviewers:          Theodore Friedmann, M.D.
David DeMets, Ph.D.

 

10:50 AM        Discussion of Human Gene Transfer Protocol #0307-594 entitled:  
A Phase Study to Determine the Safety and Biological Activity of Cell-Mediated Gene Therapy Using Tissue Gene-C in Patients with Degenerative Joint Disease of the Knee Prior to Total Knee Arthroplasty

                        PI:        Michael A. Mont, M.D., Sinai Hospital, Baltimore, MD

 

                        RAC Reviewers:          Terry Kwan

Diane Wara, M.D.

Neal DeLuca, Ph.D.


Ad Hoc Reviewers:       Robert H. Carter, M.D., University of Alabama


                        Tab 2306                     Protocol

                        Tab 2307                     OBA Summary

OBA Letter to PI on in-depth RAC Review and Public Discussion

                                                            Outcome of Initial Review by RAC Members

Reviews from Ms. Kwan, and Drs. Wara, DeLuca, Carter

            PI’s/Sponsor’s Response

 

 

12:40 PM         Public Comment


12:50 PM         LUNCH


1:50 PM          Discussion of Human Gene Transfer Protocol #0307-588 entitled:

                        A Phase I Dose Escalation Study of Intra-Articular Administration of tgAAC94, a Recombinant Adeno-Associated Vector containing the TNFR: Fc Fusion Gene in Rheumatoid Arthritis

 

                        PI:        Philip J. Mease, M.D., Swedish Hospital, Seattle, WA

 

                        RAC Reviewers:          Robert Simari, M.D.

Baruch Brody, Ph.D.

Thomas Gelehrter, M.D.

Ad Hoc Reviewers:       Robert H. Carter, M.D., University of Alabama
Christopher H. Evans, D.Sc., Ph.D., Harvard Medical School


                        Tab 2308                     Protocol

                        Tab 2309                     OBA Summary

OBA Letter to PI on in-depth RAC Review and Public Discussion

Outcome of Initial Review by RAC Members
Reviews from Drs. Simari, Brody, Gelehrter, Carter, and Evans
PI’s/Sponsor’s Response

 

3:40 PM           Public Comment


3:50 PM           BREAK

 

4:05 PM           Data Management Report

                        Tab 2310         Protocol List

                                                Protocols Not Selected for RAC Public Review

                                               

                        RAC Reviewers:          Baruch Brody, Ph.D.

                                                            Linda Gooding, Ph.D.

                                                            Larry Johnson, M.D.

                                                            Robert Simari, M.D.

                                                            Diane Wara, M.D.

 

4:20 PM           Informed Consent Working Group Update

 

4:45 PM           ADJOURNMENT

 

 

Thursday, September 18, 2003

 

8:00 AM          Call to Order and Opening Remarks

Theodore Friedmann, M.D., Chair, NIH RAC 

8:10 AM Amendments and Updates to Protocol 0010-419:  Intratumoral Injections of a Replication-Incompetent Adenoviral Vector Encoding a Factor VII Immunoconjugate to Induce a Cytolytic Immune Reponse Against Melanoma Tumors: A Pilot Trial
Speaker: Albert B. Deisseroth, M.D., Ph.D., Sidney Kimmel Cancer Center

 

9:10 AM          Discussion of Human Gene Transfer Protocol #0307-592 entitled: 
A Phase 1 Study to Determine the Safety and Immunogenicity of Vaccination with Listeria Monocytogenes Expressing Human Papilloma Virus type 16 E7 for the Treatment of Progressive, Recurrent and Advanced Squamous Cell Cancer of the Cervix

 

                        PI:        John Marshall, M.D., Georgetown University Medical Center

 

                        RAC Reviewers:          Emmett Barkley, Ph.D.

Larry Johnson, M.D.

Bernard Lo, M.D.

                                                                 

                        Tab 2311                     Protocol

                        Tab 2312                     OBA Summary

OBA Letter to PI on In-depth RAC Review and Public Discussion

                                                            Outcome of Initial Review by RAC Members

Reviews from Drs. Barkley, L. Johnson, Lo and PI’s/Sponsor’s Response

 

11:00 AM        Public Comment

 

11:10 AM        BREAK

 

11:25 AM        Global Site Preferences for MLV and HIV-1 Proviral Integration in the Human Genome

                        Speaker:           Shawn M. Burgess, Ph.D., NIH

 

12:10 PM         LUNCH

 

1:10 PM           Discussion of Human Gene Transfer Protocol #0307-593 entitled:
A Phase I Open-label Safety Study of Intrastriatal infusion of Adeno-associated virus encoding human aromatic L-amino acid decarboxylase (AAV-hAADC-2) in subjects with advanced Parkinson’s Disease [AAV-hAADC-2-003]

PI:        Michael Aminoff, M.D., D.Sc., University of California, San Francisco

 

                        RAC Reviewers:          Philip Johnson, M.D.

Martha Bohn, Ph.D.

Madison Powers, Ph.D.


                        Ad Hoc Reviewer:        Eugene Redmond, M.D., Yale University, (tel-conference)   

    

Tab 2313                     Protocol

Tab 2314                     OBA Summary

OBA Letter to PI on In-depth RAC Review and Public Discussion

                                                            Outcome of Initial Review by RAC Members

Reviews from Drs. P. Johnson, Bohn, Powers, and Redmond,

            PI’s/Sponsor’s Response

2:45 PM           Public Comment

 

3:00 PM           ADJOURNMENT